Engineered U7 snRNA mediates sustained splicing correction in erythroid cells from β-thalassemia/HbE patients

by Sarinthip Preedagasamzin, Tiwaporn Nualkaew, Tanjitti Pongrujikorn, Natini Jinawath, Ryszard Kole, Suthat Fucharoen, Natee Jearawiriyapaisarn, Saovaros Svasti
Published 2019